Treatment Plan For rhGUS (UX003) Enzyme Replacement Therapy for a MPS VII Patient under Compassionate Use
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- STATUS
- Not Recruiting
Updated on 19 February 2024
Summary
The purpose of this study is to provide access to an investigational drug called UX003 for one child diagnosed with Mucopolysaccharidosis 7 (MPS VII or Sly syndrome)
Description
The purpose of this study is to provide access to an investigational drug called UX003 for one child diagnosed with Mucopolysaccharidosis 7 (MPS VII or Sly syndrome)
Details
| Condition | Mucopolysaccharidosis 7 |
|---|---|
| Age | 100years or below |
| Clinical Study Identifier | TX7883 |
| Last Modified on | 19 February 2024 |
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